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Physiology and Medicine

Improved & New Gene Therapy Delivery Vehicles

Develop improved gene therapy vectors that can be manufactured at scale, as well as completely novel therapeutic gene therapy delivery vehicles. 

Resources (3)

Siren Biotechnology
Company
Active Genetics Comes Alive
Research and Reviews
Gene Therapy for Common Diseases
Whitepapers and Essays

R&D Gaps (1)

We Can’t Safely and Controllably Deliver Complex Molecular Payloads to the Targets We Want in the Body

Physiology and Medicine
Current in-vivo delivery systems (viral vectors, nanoparticles, microchips) face challenges such as off-target accumulation and inefficiency, particularly in delivering therapies to the brain. Novel delivery approaches are needed to improve targeting and performance.
Physiology and Medicine
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